Reducing Patient Burden While Maintaining High-Frequency Monitoring in a Hemophilia Gene Therapy Trial

Reducing Patient Burden While Maintaining High-Frequency Monitoring in a Hemophilia Gene Therapy Trial Image Balancing rigorous clinical oversight with patient accessibility is critical in complex gene therapy trials. Intensive early-phase monitoring and complex protocols can place significant burden on patients, impacting recruitment, retention, and overall study success. This case study explores how a decentralized clinical trial model supported high-frequency safety monitoring while reducing patient burden, improving access, and driving strong long-term engagement. 
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