Clinical Trials: The Bridge to an Optimal Registration


Tuesday, Oct 29
Leiden University Medical Center
Room 2 - Building 1
The Netherlands

Join ProPharma Group for our seminar on Clinical Trials: The Bridge to an Optimal Registration! 

Professor Doctor Annemieke Aartsma-Rus
Professor of translational genetics
Department of human genetics, LUMC

Will your clinical development deliver new treatment options? Solid science will always be a foundation, but a successful development process stretches beyond scientific opportunities. Find the gaps and apply a lifecycle approach for product development. Drinks and snacks will be provided.  Join our seminar!

Professor Doctor Annemieke Aartsma-Rus will share lessons learned from the failure of a registration trials on a Duchenne muscular dystrophy treatment. Step into the world of Phase II studies based on a multidisciplinary approach and strategy building. Discuss topics such as dose finding, comparator picking, epidemiology, and dosing formulations. Focus on small (Phase II/III) studies on rare diseases.

Program

16.30 Doors open
17.00 Welcome
17.15 – 18.15 Annemieke Aartsma-Rus (Professor of translational genetics, LUMC), Therapy development for rare diseases takes more than a therapeutic compound
18.15 – 19.00 Thomas de Vlaam (Founder and CEO, Amylon Therapeutics): Industry perspective
19.00 – 19.30 ProPharma Group: Regulatory affairs
19.30 Drinks & Networking
20.30 Close

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