Join ProPharma Group for our seminar on Clinical Trials: The Bridge to an Optimal Registration!
Will your clinical development deliver new treatment options? Solid science will always be a foundation, but a successful development process stretches beyond scientific opportunities. Find the gaps and apply a lifecycle approach for product development. Drinks and snacks will be provided. Join our seminar!
Professor Doctor Annemieke Aartsma-Rus will share lessons learned from the failure of a registration trials on a Duchenne muscular dystrophy treatment. Step into the world of Phase II studies based on a multidisciplinary approach and strategy building. Discuss topics such as dose finding, comparator picking, epidemiology, and dosing formulations. Focus on small (Phase II/III) studies on rare diseases.
16.30 Doors open
17.15 – 18.15 Annemieke Aartsma-Rus (Professor of translational genetics, LUMC), Therapy development for rare diseases takes more than a therapeutic compound
18.15 – 19.00 Thomas de Vlaam (Founder and CEO, Amylon Therapeutics): Industry perspective
19.00 – 19.30 ProPharma Group: Regulatory affairs
19.30 Drinks & Networking